Sarepta Seeks Broader Approval for Gene Therapy Even After Drug Trial Fizzled
Normally when a drug fails to show a clear effect in a final-stage trial, the company developing it
2023-11-01 05:15
Gene Therapy for Kids’ Deadly Muscle Disease Fails to Reach Trial Goal
Roche Holding AG shares dropped after a trial of its gene therapy for Duchenne muscular dystrophy did not
2023-10-31 16:58
Drug Companies Are Minting Billions on Unproven Treatments With FDA Shortcut
When Exondys 51 was approved to treat Duchenne muscular dystrophy, a deadly disease that puts kids in wheelchairs
2023-05-15 07:16